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Adult Neuronal Ceroid Lipofuscinosis - 21 Studies Found
Estado | Estudiar |
Recruiting |
Nombre del estudio: Clinical and Neuropsychological Investigations in Batten Disease Condición: Neuronal Ceroid Lipofuscinosis Fecha: 2013-05-17 |
Terminated |
Nombre del estudio: Collection of Cerebrospinal Fluid in Healthy Children Condición:
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Recruiting |
Nombre del estudio: Batten CLN6 Gene Therapy Condición:
Fecha: 2016-03-16 Intervenciones: Drug: scAVV9.CB.CLN6 Six subjects with diagnosis of CLN6 disease will receive scAVV9.CB.CLN6 administere |
Completed |
Nombre del estudio: Genotype - Phenotype Correlations of LINCL Condición:
Fecha: 2005-09-06 |
Active, not recruiting |
Nombre del estudio: A Multicenter, Multinational, Extension Study to Evaluate the Long-Term Efficacy and Safety of BMN 190 in Patients With CLN2 Disease Condición:
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Enrolling by invitation |
Nombre del estudio: A Safety, Tolerability, and Efficacy Study of Intracerebroventricular BMN 190 in Pediatric Patients < 18 Years of Age With CLN2 Disease Condición:
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Recruiting |
Nombre del estudio: Genetic Characterization of Movement Disorders and Dementias Condición:
Fecha: 2015-04-03 |
Recruiting |
Nombre del estudio: UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells Condición:
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Recruiting |
Nombre del estudio: Human Placental-Derived Stem Cell Transplantation Condición:
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